Currently, there are many devastating and orphan diseases that remain a challenge to treat. Many biotechnology companies are working hard and investing heavily in developing therapies that can manage human genetic diseases. Amicus Therapeutics is a global biopharmaceutical company that is in the frontline in developing therapies that treat these rare and orphan diseases. The company products are manufactured using high technology to ensure they are effective.
Amicus Therapeutics targets lysosomal Storage disorders, genetic connective skin disorder as well as Pompe disease patients. The biotechnology company aims to make a difference in patients’ lives by providing reliable treatment options for these diseases. The company develops products based on the Chaperone-advance replacement therapy platform. On top of that, Amicus concentrates on enzyme replacement therapies developments. They have a team of experts who use latest technologies in all their production processes.
Amicus has produced many effective treatments. Migalastat is one of them and isa personalized medicine that is effective in helping patients with Fabry disease. This is dependent on patients’ genetic diagnosis (HighTechChronicle). They have also developed another therapy that targets genetic connective tissues disorder. SD-101 is an effective medicine developed to treat Epidermolysis Bullosa. On topof that Amicus Therapeutics manufacture products that treat Pompe disease as well as several other Lysosomal Storage Disorders.
Amicus uses innovative and more advance technology to develop high-quality treatments specifically targeting mutated proteins. With highly experienced scientists who have the interest of patients suffering from these diseases, their products don’t disappoint. The company invests heavily in research to be able to understand these diseases and in return develop treatments that are disease specific. The company also listens and learned from individuals affected by these diseases. Amicus Therapeutics also have many tactics that help support patients and their families. They also educate and advocate on behalf of Fabry and Pompe diseases (https://www.indeed.com/q-Amicus-Therapeutics-l-Cranbury,-NJ-jobs.html).
Amicus Therapeutics has had great leadership from their leaders. They have ensured that everything is done according to stipulated health standards. On top of that, the biotechnology company has been receiving grants. The Michael J. Fox Foundation and Alzheimer’s Drug Discovery Foundation are some of the organizations that have supported Amicus Therapeutics.